Job Description
Why Join Us?
Be a hero for our rare disease patients
At Ultragenyx, we fundamentally believe that taking real impactful action to care for the needs of patients and our people is always the right thing to do. To achieve this goal, our vision is to lead the future of rare disease medicine. For us, this means going where other biopharma companies won’t go – challenging the status quo and creating a new model that advances our field so more patients and caregivers can benefit from life-changing treatments. We do this by following the science, applying a novel rapid development approach, making innovative medicines at fair and reasonable prices, and creating a collaborative ecosystem to reach patients in ways that are most meaningful for them.
Our commitment and care for patients extends to our people, so culture is an essential cornerstone for Ultragenyx. We remain continuously focused on creating a supportive and inclusive environment of profound learning and growth – so employees can thrive in all areas of their lives, in and outside of work. Ultimately, we want to be an organization where we would be proud for our family, friends and children to work.
If you want to have a meaningful impact, do the best work of your career, and grow a lot, both professionally and personally, come join our team .
Position Summary:
ultra dedicated – Your biggest challenges yield rare possibilities
Ultragenyx is seeking a dynamic and experienced leader to join the Global Medical Affairs team with responsibility for the pipeline portfolio. The Sr. Director, Pipeline Lead will provide strategic early medical affairs leadership across multiple early-stage assets in our neurology and inborn errors of metabolism portfolios, including, for example, GNE Myopathy, Creatine Transporter Deficiency, Wilson’s Disease, and Ornithine Transcarbamylase Deficiency. This role requires an adaptable leader willing to take a “hands on” approach in their work and who is comfortable working in a fast-paced intellectual environment.
Work Model:
Remote: Officially documented as working full-time from home, with travel to Ultragenyx’s offices or other locations on occasion as needed.
Responsibilities:
Provide early medical affairs leadership to assigned programs, serving as an active core member of the Program Team and decision-making sub-teams, and contributing to the progression of program milestones
Demonstrate and apply deep rare disease expertise across assigned programs, actively building and maintaining a global network of therapeutic area experts. Lead insight-generation activities, including scientific advisory boards and steering committees that inform program strategy
Lead the development of an aligned early-stage Integrated Evidence Generation Strategy for assigned programs, incorporating real world evidence generation, ensuring plans are strategically designed and executed to establish a robust foundational scientific evidence base
Lead proactive competitive landscape assessments and translate emerging science and therapeutic area dynamics into strategic recommendations for asset positioning
Establish and lead the Global Medical Sub Team(s), and drive the development and implementation of the medical strategy for assigned pipeline programs, aligned with program objectives and through close collaboration with global medical functions and regional medical leads
Partner with scientific and medical communications to guide development of the end-to-end scientific communication platform, including the global scientific narrative, ensuring a consistent external global scientific education strategy
Ensure timely and effective data dissemination by leading publication strategies, congress planning, and scientific education initiatives
Provide deep disease area and product expertise, ensuring accurate and consistent communication of clinical and scientific data, including sign off in review committees
Provide guidance, tools, and high-quality compliant training to US field and regional medical affairs teams to elevate consistent scientific exchange, and other internal teams as needed
Collaborate effectively with clinical development, HEOR, diagnostics, scientific and medical communications and publications, regulatory, market access, commercial, training, and patient advocacy to influence strategic decision making and advance program initiatives
Requirements:
Advanced medical/scientific degree (MD, DO, PhD, PharmD) (required)
Minimum 7 years of experience in Medical Affairs (required); global experience is strongly preferred
Proven track record in pipeline strategy, evidence generation, and external engagement
Experience and comfort operating across early-phase development programs spanning multiple disease areas
Strong collaboration and stakeholder management skills; adept at functioning in a highly matrixed environment
Recognized scientific authority with the ability to engage in advanced scientific and clinical discussions with both internal and external experts
High aptitude for attention to detail, commitment to high-quality work, and a sense of passion and urgency to achieve goals and improve the lives of patients
Highly analytical and strategic thinker with the ability to identify interdependencies, consider medical implications, and understand the broader goals of a program
Excellent communication skills, with the ability to effectively articulate scientific and strategic concepts in both written documents and verbal presentations
Travel estimated up to 15%
#LI-CS1 #LI-Remote
The typical annual salary range for this full-time position is listed below. This range reflects the characteristics of the job, such as required skills and qualifications and is based on the office location noted in this job posting. The range may also be adjusted based on applicant’s geographic location.
This position is eligible for annual bonus and equity incentives. Actual individual pay is determined by demonstrated experience and internal equity alignment.
Pay Range
$270,500—$334,100 USD
Full Time employees across the globe enjoy a range of benefits, including, but not limited to:
· Generous vacation time and public holidays observed by the company
· Volunteer days
· Long term incentive and Employee stock purchase plans or equivalent offerings
· Employee wellbeing benefits
· Fitness reimbursement
· Tuition sponsoring
· Professional development plans
\* Benefits vary by region and country
Ultragenyx Pharmaceutical is an equal opportunity employer and prohibits unlawful discrimination based on race, color, religion, gender, sexual orientation, gender identity/expression, national origin/ancestry, age, disability, marital and veteran status, and any other status or classification protected by applicable federal, state, and/or local laws. Reasonable accommodation will be provided for all protected statuses or classifications protected by applicable law, including individuals with disabilities, disabled veterans, for pregnancy, childbirth, and related medical conditions, and based on sincerely held religious beliefs. Applicants can request an accommodation prior to accepting a job offer. If you require reasonable accommodation in completing this application, or in any part of the recruitment process, you may contact Talent Acquisition by emailing us at [email protected] .
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It is unlawful in Massachusetts to require or administer a lie detector test as a condition of employment or continued employment. An employer who violates this law shall be subject to criminal penalties and civil liability.
Note to External Recruiters: All candidate activity and open positions are managed strictly through our Human Resources Department. Our Human Resources Department kindly requests that recruiters not contact employees/hiring managers directly in an attempt to solicit business and present candidates. Please note that failure to comply with this request will be a factor in determining a professional relationship with our organization. Submission of unsolicited resumes prior to an agreement set in place between the Human Resources Department and the recruiting agency will not create any implied obligation. Inquiries on developing a recruiting relationship with us, may be directed to : [email protected] .
